About Krabbe Disease Treatment
Krabbe disease is an autosomal recessive genetic disorder. Krabbe disease is an uncommon inherited nerve system ailment that usually leads to death. Krabbe disease is caused by a lack of galactosylceramidase, which causes severe degradation of the myelin sheaths that encase nerves in the brain. Krabbe illness affects 85 to 90 percent of children under the age of six months, but it can also strike later in life. A genetic mutation, or a permanent change in the DNA sequence that makes up a gene, causes Krabbe disease. The product for which the gene codes is affected by the mutation.
Attributes | Details |
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Study Period | 2018-2030 |
Base Year | 2023 |
Unit | Value (USD Million) |
The global market is highly competitive and consists of a limited number of providers who compete with each other. The intense competition, changing consumer spending patterns, demographic trends, and frequent changes in consumer preferences pose significant opportunities for market growth. Analyst at AMA Research estimates that United States Players will contribute the maximum growth to Global Krabbe Disease Treatment market throughout the forecasted period. Established and emerging Players should take a closer view at their existing organizations and reinvent traditional business and operating models to adapt to the future.
Polpharma (Poland), Sanofi S.A. (France), Takeda Pharmaceutical Company Limited (Japan), Teva Pharmaceutical Industries Ltd., (Israel), UCB Pharmaceuticals (Belgium), Zhejiang Jiuzhou Pharmaceuticals Co Ltd (China), Abbott Laboratories (United States), GlaxoSmithKline Plc (United Kingdom), Novartis AG (Switzerland) and Johnson & Johnson Services Inc (United States) are some of the key players that are part of study coverage. Additionally, the Players which are also part of the research coverage are Pfizer (United States).
Segmentation Overview
AMA Research has segmented the market of Global Krabbe Disease Treatment market by Type (Infantile (occurs in babies less than six months of age) and Late-onset (can happen at any other time)) and Region.
On the basis of geography, the market of Krabbe Disease Treatment has been segmented into South America (Brazil, Argentina, Rest of South America), Asia Pacific (China, Japan, India, South Korea, Taiwan, Australia, Rest of Asia-Pacific), Europe (Germany, France, Italy, United Kingdom, Netherlands, Rest of Europe), MEA (Middle East, Africa), North America (United States, Canada, Mexico). If we see Market by Diagnosed Test, the sub-segment i.e. Imaging Scans (MRI) will boost the Krabbe Disease Treatment market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth. If we see Market by Symptoms, the sub-segment i.e. Frequent Vomiting will boost the Krabbe Disease Treatment market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth.
Influencing Trend:
Emergence of Pharmacological Chaperone Therapy
Market Growth Drivers:
Increase in Clinical Development of the Treatment for the Krabbe Disease and Highly Developed Technologies and Innovative Drugs for Management of Krabbe Disease
Challenges:
Limited Patient Pool for Clinical Trial
Restraints:
High Cost Associated with Treatment
Opportunities:
Rise in Investment in R & D
Market Leaders and their expansionary development strategies
In 2021, Pfizer announced that it had entered into a definitive agreement to acquire Arena Pharmaceuticals, a clinical stage company specializing in therapies treating immuno-inflammatory diseases, for USD 6.7 billion dollars.
Key Target Audience
Venture Capitalists and Private Equity Firms, Government Bodies, Corporate Entities, Government and Private Research Organizations and Others
About Approach
To evaluate and validate the market size various sources including primary and secondary analysis is utilized. AMA Research follows regulatory standards such as NAICS/SIC/ICB/TRCB, to have a better understanding of the market. The market study is conducted on basis of more than 200 companies dealing in the market regional as well as global areas with the purpose to understand the companies positioning regarding the market value, volume, and their market share for regional as well as global.
Further to bring relevance specific to any niche market we set and apply a number of criteria like Geographic Footprints, Regional Segments of Revenue, Operational Centres, etc. The next step is to finalize a team (In-House + Data Agencies) who then starts collecting C & D level executives and profiles, Industry experts, Opinion leaders, etc., and work towards appointment generation.
The primary research is performed by taking the interviews of executives of various companies dealing in the market as well as using the survey reports, research institute, and latest research reports. Meanwhile, the analyst team keeps preparing a set of questionnaires, and after getting the appointee list; the target audience is then tapped and segregated with various mediums and channels that are feasible for making connections that including email communication, telephonic, skype, LinkedIn Group & InMail, Community Forums, Community Forums, open Survey, SurveyMonkey, etc.