Industry Background:
Dravet syndrome is a rare disease and a severe form of epilepsy that is a part of the group of diseases known as SCN1A-related seizure disorders. It occurs due to a mutation in the SCN1A gene, which is required for the proper function of brain cells. The condition appears during the first year of life as febrile seizures. As the condition progresses, other types of seizures typically occur, including myoclonus and status epilepticus. The mortality rate of DS is high, with 15% of patients dying by adolescence and 20% by early adulthood. Moreover, there is no cure for Dravet syndrome but most treatments aim to reduce seizures. But there are anti-epileptic medications available i.e. first line anti-seizure medications, Second line anti-epileptic medications and third line anti-epileptic medications treatments for DS. Seizures in DS is difficult to manage but can be reduced by anticonvulsant medications such as Clobozam, Stiriptenol, valproate etc. As the disorder varies from individual to individual, treatment protocols may vary. A diet high in fats and low in carbohydrate may be beneficial known as Ketogenic diet.
Attributes | Details |
---|
Study Period | 2019-2029 |
Base Year | 2023 |
Unit | Value (USD Million) |
Key Companies Profiled | Biocodex (United Kingdom), Epygenix Therapeutics, Inc. (United States), GW Pharmaceuticals Plc. (United Kingdom), Ovid Therapeutics (United States), Takeda Pharmaceutical Company Ltd (Japan), OPKO Health Inc. (United States), Zogenix, Inc. (United States), PTC Therapeutics, Inc. (United States), Biscayne Neurotherapeutics, Inc. (Supernus Pharmaceuticals) (United States) and Pfizer Inc. (United States) |
This growth is primarily driven by Rising Number of Treatment Strategies, Increasing Research and Development Activities and Rising Prevalence of Rare Disease.
Globally, a noticeable market trend is evident Strong Drug Pipeline for the Treatment
Major Players, such as Biocodex (United Kingdom), Epygenix Therapeutics, Inc. (United States), GW Pharmaceuticals Plc. (United Kingdom), Ovid Therapeutics (United States), Takeda Pharmaceutical Company Ltd (Japan), OPKO Health Inc. (United States), Zogenix, Inc. (United States), PTC Therapeutics, Inc. (United States), Biscayne Neurotherapeutics, Inc. (Supernus Pharmaceuticals) (United States) and Pfizer Inc. (United States), etc have either set up their manufacturing facilities or are planning to start new provision in the dominated region in the upcoming years. Most of the key players in the global dravet syndrome treatment market are projected to enter into joint collaboration in order to consolidate their market position and develop into new business territories. Many vendors are engaging in mergers and acquisitions to fortify their position in the global dravet syndrome treatment market. Several international and regional key players are vying for their share of the market, and players must differentiate themselves to gain vital traction over their peers.
Key Developments in the Market:
In July , 2019 Epygenix Therapeutics, Inc., a privately held biopharmaceutical company developing precision medicines for Dravet Syndrome, announced today that the Company has received an Investigational New Drug Application (IND) approval from the U.S. Food and Drug Administration (FDA) for the treatment of patients with Dravet syndrome.
In Jul.2023-- Stoke Therapeutics, Inc. (Nasdaq: STOK), a biotechnology company dedicated to addressing the underlying cause of severe diseases by upregulating protein expression with RNA-based medicines, today announced positive new safety and efficacy data from patients treated with STK-001 in the two ongoing Phase 1/2a studies (MONARCH and ADMIRAL) and the SWALLOWTAIL open-label extension (OLE) study in children and adolescents with Dravet syndrome.
Influencing Trend:
Strong Drug Pipeline for the Treatment and Increased Use of New Generation Drugs
Market Growth Drivers:
Rising Number of Treatment Strategies, Increasing Research and Development Activities and Rising Prevalence of Rare Disease
Challenges:
Poor Healthcare System in Low and Middle-Income Countries
Restraints:
Low Awareness among Patients
Opportunities:
Highly Focused Innovation in Product Technologies and Advancement in Biomedical Sciences
AMA Research follows a focused and realistic research framework that provides the ability to study the crucial market dynamics in several regions across the world. Moreover, an in-depth assessment is mostly conducted by our analysts on geographical regions to provide clients and businesses the opportunity to dominate in niche markets and expand in emerging markets across the globe. This market research study also showcases the spontaneously changing Players landscape impacting the growth of the market. Furthermore, our market researchers extensively analyze the products and services offered by multiple players competing to increase their market share and presence.
Customization in the Report
AMA Research features not only specific market forecasts but also includes significant value-added commentary on:
- Market Trends
- Technological Trends and Innovations
- Market Maturity Indicators
- Growth Drivers and Constraints in Dravet Syndrome Treatment Market
- Analysis about New Entrants in Dravet Syndrome Treatment Market & Entry/Exit Barriers
- To Seize Powerful Market Opportunities
- Identify Key Business Segments, Market Proposition & Gap Analysis
- An Unbiased Perspective towards Market Performance & Indicators
Against this Challenging Backdrop, Dravet Syndrome Treatment Study Sheds Light on
The Dravet Syndrome Treatment Market status quo and key characteristics. To end this, Analysts at AMA organize and took surveys of the Dravet Syndrome Treatment industry Players. The resultant snapshot serves as a basis for understanding why and how the industry can be expected to change.
Where Dravet Syndrome Treatment industry is heading and what are the top priorities. Insights are drawn from financial analysis, surveys, and interviews with key executives and industry experts.
How every company in this diverse set of Players can best navigate the emerging competition landscape and follow a strategy that helps them position to hold the value they currently claim or capture the new addressable opportunity.