About Argininemia Treatment
Argininemia (ARG) is a disorder in which dangerous levels of arginine and ammonia accumulate in the body. It is classified as an amino acid disorder because persons with ARG are unable to break down arginine, an amino acid, a tiny molecule that builds up proteins. Treatment for arginine mix is nutritional, including protein restriction and amino acid supplementation. Individuals with arginine mix can typically live healthily lives if the illness is diagnosed early and effective therapy is undertaken. Argininemia is a rare disorder and few patients have been treated from an early age, prior to onset of disabling symptoms. Dietary restriction of protein is the basic treatment, with supporting therapy to prevent and control the hyperammonemia. Because the diagnosis and therapy of argininemia is complex, the pediatrician is advised to manage the patient in close collaboration with a consulting pediatric metabolic disease specialist. It is recommended that parents travel with a letter of treatment guidelines from the patient’s physician.
Attributes | Details |
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Study Period | 2018-2028 |
Base Year | 2022 |
Unit | Value (USD Million) |
The demand for Argininemia Treatment is increasing due to its rising progressive and devastating nature with each passing day. The Companies in this industry are facing fierce competition. Many global and regional service providers compete directly with industry leaders in this field. It has been identified that market-leading players are investing heavily in technological development, resource utilization to boost the market position. Analyst at AMA Research estimates that United States Players will contribute the maximum growth to Global Argininemia Treatment market throughout the forecasted period. Established and emerging Players should take a closer view at their existing organizations and reinvent traditional business and operating models to adapt to the future.
BabyFirst (United States), Invitae (United States), TriHealth (United States), Aeglea Bio Therapeutics Inc (United States), Sigma-Aldrich (United States), R & D Systems (United States), ACROBiosystems (United States) and Breda Genetics srl (Italy) are some of the key players that are part of study coverage. Additionally, the Players which are also part of the research coverage are Orphanet (France), Mendelian Health (United Kingdom), Asbbs (United States), Novus Biologicals (United States) and VarSome (China).
Segmentation Overview
AMA Research has segmented the market of Global Argininemia Treatment market by Type (Oral and Injection) and Region.
On the basis of geography, the market of Argininemia Treatment has been segmented into South America (Brazil, Argentina, Rest of South America), Asia Pacific (China, Japan, India, South Korea, Australia, Rest of Asia-Pacific), Europe (Germany, France, Italy, United Kingdom, Netherlands, Rest of Europe), MEA (Middle East, Africa), North America (United States, Canada, Mexico). If we see Market by End Users, the sub-segment i.e. Hospitals will boost the Argininemia Treatment market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth. If we see Market by Category, the sub-segment i.e. Congenital and Genetic Diseases will boost the Argininemia Treatment market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth. If we see Market by Treatment, the sub-segment i.e. Dietary Proteins will boost the Argininemia Treatment market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth.
Influencing Trend:
The Emergence of Lipid Nanoparticle-Targeted mRNA Therapy
Market Growth Drivers:
Increasing Incidents of Urea Cycle Disorders and Rising Awareness of Argininemia
Challenges:
Lack of Awareness Regarding Argininemia Treatment and Argininemia Treatment is Very Expensive
Restraints:
Argininemia Treatment May Cause Some Side Effects Such as Poor Growth and Stiff Muscles
Opportunities:
Rise in Ammonia Deficiency in Babies and Emerging Technologies and Precision Medicine
Market Leaders and their expansionary development strategies
In May 2023, Horizon Therapeutics acquires Metanomics, gaining access to investigational gene therapy MT007 for argininemia. This acquisition brings MT007, a potentially curative gene therapy, closer to the market, offering a long-term treatment option for argininemia patients.
In March 2023, BioMarin Pharmaceuticals receives FDA approval for Palynziq (pegdefibrotide) oral granules for the treatment of argininemia. This groundbreaking approval provides a convenient and easier-to-administer option for patients, replacing the previously available injectable form of pegdefibrotide.
Key Target Audience
Venture and Capitalist, Raw Materials Suppliers, New Entrants/Investors, Healthcare and End-Use Industries
About Approach
To evaluate and validate the market size various sources including primary and secondary analysis is utilized. AMA Research follows regulatory standards such as NAICS/SIC/ICB/TRCB, to have a better understanding of the market. The market study is conducted on basis of more than 200 companies dealing in the market regional as well as global areas with the purpose to understand the companies positioning regarding the market value, volume, and their market share for regional as well as global.
Further to bring relevance specific to any niche market we set and apply a number of criteria like Geographic Footprints, Regional Segments of Revenue, Operational Centres, etc. The next step is to finalize a team (In-House + Data Agencies) who then starts collecting C & D level executives and profiles, Industry experts, Opinion leaders, etc., and work towards appointment generation.
The primary research is performed by taking the interviews of executives of various companies dealing in the market as well as using the survey reports, research institute, and latest research reports. Meanwhile, the analyst team keeps preparing a set of questionnaires, and after getting the appointee list; the target audience is then tapped and segregated with various mediums and channels that are feasible for making connections that including email communication, telephonic, skype, LinkedIn Group & InMail, Community Forums, Community Forums, open Survey, SurveyMonkey, etc.