Global Spinal Muscular Atrophy Market Overview:
Spinal Muscular Atrophy (SMA) is also known as spinal muscle wasting, spinal amyotrophies, or spinal muscle degeneration. It is a group of inherited diseases that affects the functioning of muscles because of deterioration. SMA leads to weakness affecting motor neurons present in the brain & spinal cord and may even result in death. The muscle weakness usually worsens with age. As per the survey, spinal muscular atrophy affects 1 per 8,000 to 10,000 people worldwide. Spinal muscular atrophy type I is the most common type, accounting for about half of all cases followed by Type II and Type III. Although it is not currently possible to cure Spinal Muscular Atrophy, ongoing research to find new treatments is expected to open new opportunities for the market in the coming years and Gene therapy is a treatment alternative to drugs.
As per latest study released by AMA Research, the Global Spinal Muscular Atrophy market is expected to see growth rate of 12.8%Attributes | Details |
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Study Period | 2017-2027 |
Base Year | 2021 |
Forecast Period | 2022-2027 |
Historical Period | 2017-2021 |
Unit | Value (USD Million) |
High Growth Market | Asia Pacific |
Customization Scope | Avail customization with purchase of this report. Add or modify country, region & or narrow down segments in the final scope subject to feasibility |
Growth Drivers
- Growing Adoption Of Spinraza
- Increasing Spinal Muscular Atrophy Cases In Children
Roadblocks
- Limited Access To Spinal Muscular Atrophy Treatment
Opportunities
- Increasing Awareness About Spinal Muscular Atrophy Due to Initiatives Undertaken By Government and Nonprofit, Organizations
- Opportunities from Untapped Countries
Challenges
- Unavailability of Regulations for Spinal Muscular Atrophy Treatments
Competitive Landscape:
The market appears to be highly concentrated and only Biogen has approved drugs for spinal muscular atrophy treatment. However, it is expected that new players will be entering the market during the forecast period. The increase in the development of new innovative therapies and investment in R& D by companies will increase the competition level in the forecast period.
Some of the key players profiled in the report are Biogen Idec (United States), Pfizer (United States), Isis Pharmaceuticals (United States), Boehringer Ingelheim (Germany), F. Hoffmann-La Roche (Switzerland) and Regeneron Pharmaceuticals (United States). Analyst at AMA Research see United States and European Players to retain maximum share of Global Spinal Muscular Atrophy market by 2027. Considering Market by Treatment, the sub-segment i.e. Gene Therapy will boost the Spinal Muscular Atrophy market. Considering Market by Administration Route, the sub-segment i.e. Oral will boost the Spinal Muscular Atrophy market.
In August 2020, FDA approved Roche’s Spinal Muscular Atrophy Drug named Risdiplam (Evrysdi), a first oral therapy drug. Evrysdi is the first drug for spinal muscular atrophy disease that can be taken orally.
What Can be Explored with the Spinal Muscular Atrophy Market Study
Gain Market Understanding
Identify Growth Opportunities
Analyze and Measure the Global Spinal Muscular Atrophy Market by Identifying Investment across various Industry Verticals
Understand the Trends that will drive Future Changes in Spinal Muscular Atrophy
Understand the Competitive Scenario
- Track Right Markets
- Identify the Right Verticals
Research Methodology:
The top-down and bottom-up approaches are used to estimate and validate the size of the Global Spinal Muscular Atrophy market.
In order to reach an exhaustive list of functional and relevant players various industry classification standards are closely followed such as NAICS, ICB, SIC to penetrate deep in important geographies by players and a thorough validation test is conducted to reach most relevant players for survey in Spinal Muscular Atrophy market.
In order to make priority list sorting is done based on revenue generated based on latest reporting with the help of paid databases such as Factiva, Bloomberg etc.
Finally the questionnaire is set and specifically designed to address all the necessities for primary data collection after getting prior appointment by targeting key target audience that includes New Entrants/Investors, Analysts and Strategic Business Planners, Spinal Muscular Atrophy Providers, Venture Capitalists, Private Equity Firms, Government Regulatory, Research Organizations and End Users.
This helps us to gather the data related to players revenue, operating cycle and expense, profit along with product or service growth etc.
Almost 70-80% of data is collected through primary medium and further validation is done through various secondary sources that includes Regulators, World Bank, Association, Company Website, SEC filings, OTC BB, USPTO, EPO, Annual reports, press releases etc.