List of companies from research coverage that are profiled in the study
- Adverum Biotechnologies (United States)
- BioMarin Pharmaceutical Inc. (United States)
- Biovista Inc. (United States)
- Cardero Therapeutics Inc (United States)
- Catabasis Pharmaceuticals, Inc. (United States)
- Forward Pharma A/S (Denmark)
- Ixchel Pharma LLC (United States)
- Pfizer Inc (United States)
- ProQR Therapeutics NV (Netherlands)
- Reata Pharmaceuticals Inc. (United States)
- Retrotope Inc (United States)
- Shire Plc (United States)
Additional players considered in the study are as follows:
STATegics, Inc. (United States)
,
Voyager Therapeutics Inc (United States)