Industry Background:
Duchenne muscular dystrophy is a medical condition that develops due to a shortage of protein called “dystrophin”. It causes deterioration and breaks down muscles, which results in walking difficulty and limited general mobility. Duchenne muscular dystrophy is considered as one of the most progressive childhood neuromuscular disorders. Duchenne muscular dystrophy (DMD) is a genetic disorder characterized by progressive muscle degeneration and weakness. It is a rare muscle disease, which majorly affects males. There are novel drugs and therapies, disease-modifying, and mutation-specific therapies that are some of the emerging major breakthroughs in the DMD treatment market. it affects boys mostly, but few cases of girls have been registered too.
Attributes | Details |
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Study Period | 2019-2029 |
Base Year | 2023 |
High Growth Market | Asia Pacific |
Unit | Value (USD Million) |
Key Companies Profiled | BioMarin (United States), Bristol-Myers Squibb Company (United States), Fibrogen Inc. (United States), Eli Lilly and Company (United States), Nobelpharma Co. Ltd (Japan), NS Pharma Inc. (United States), Pfizer Inc. (United States) and PTC Therapeutics (United States) |
This growth is primarily driven by High Demand for Nonsteroidal Anti-inflammatory Drugs (NSAIDs) and Rising Prevalence of Chronic Diseases.
Globally, a noticeable market trend is evident Increasing Awareness Campaigns for DMD
The Diseases & Therapeutic Areas sector in the North America region has been increasing at a sustainable rate, and further growth is expected to be witnessed over the forecast period, owing to the robust investments and expansion in production facilities in the region. Major Players, such as BioMarin (United States), Bristol-Myers Squibb Company (United States), Fibrogen Inc. (United States), Eli Lilly and Company (United States), Nobelpharma Co. Ltd (Japan), NS Pharma Inc. (United States), Pfizer Inc. (United States) and PTC Therapeutics (United States), etc have either set up their manufacturing facilities or are planning to start new provision in the dominated region in the upcoming years. With increasing campaigns and awareness programs, the number of patients is expected to come down, and hence, many companies are conducting campaign programs that help to improve focus on medicines for DMD treatment. There are also very few companies for new drug research for rare diseases because it needs bigger funds. Therefore, the market is not well established in many other therapeutic areas. However, it is expected to experience high growth and expand during the forecast period.
Key Developments in the Market:
In July , 2023 NS Pharma, Inc. announced today the U.S. Food & Drug Administration (FDA) has granted Breakthrough Therapy Designation to NS-089/NCNP-02, an investigational candidate for patients with Duchenne muscular dystrophy amenable to exon 44 skipping therapy.
In April , 2023, REGENXBIO Inc. announced that the U.S. Food and Drug Administration (FDA) has granted Fast Track designation for RGX-202, a potential one-time gene therapy for the treatment of Duchenne muscular dystrophy (Duchenne).
Influencing Trend:
Increasing Awareness Campaigns for DMD and Rising Disease Burden of Duchenne Muscular Dystrophy (DMD)
Market Growth Drivers:
High Demand for Nonsteroidal Anti-inflammatory Drugs (NSAIDs) and Rising Prevalence of Chronic Diseases
Challenges:
Stringent Government Regulations and Increasing Concern Related High Product Cost
Restraints:
Lack of Standardization to Measure Clinical Efficacy Across All Stages of DMD
Opportunities:
Upsurging Investments in Biopharmaceutical R&D to Release Novel Disease Therapies and Increasing Awareness among People and With the Government’s Urgency for the Treatment of the Disease
AMA Research follows a focused and realistic research framework that provides the ability to study the crucial market dynamics in several regions across the world. Moreover, an in-depth assessment is mostly conducted by our analysts on geographical regions to provide clients and businesses the opportunity to dominate in niche markets and expand in emerging markets across the globe. This market research study also showcases the spontaneously changing Players landscape impacting the growth of the market. Furthermore, our market researchers extensively analyze the products and services offered by multiple players competing to increase their market share and presence.
Customization in the Report
AMA Research features not only specific market forecasts but also includes significant value-added commentary on:
- Market Trends
- Technological Trends and Innovations
- Market Maturity Indicators
- Growth Drivers and Constraints in Duchenne Muscular Dystrophy Market
- Analysis about New Entrants in Duchenne Muscular Dystrophy Market & Entry/Exit Barriers
- To Seize Powerful Market Opportunities
- Identify Key Business Segments, Market Proposition & Gap Analysis
- An Unbiased Perspective towards Market Performance & Indicators
Against this Challenging Backdrop, Duchenne Muscular Dystrophy Study Sheds Light on
The Duchenne Muscular Dystrophy Market status quo and key characteristics. To end this, Analysts at AMA organize and took surveys of the Duchenne Muscular Dystrophy industry Players. The resultant snapshot serves as a basis for understanding why and how the industry can be expected to change.
Where Duchenne Muscular Dystrophy industry is heading and what are the top priorities. Insights are drawn from financial analysis, surveys, and interviews with key executives and industry experts.
How every company in this diverse set of Players can best navigate the emerging competition landscape and follow a strategy that helps them position to hold the value they currently claim or capture the new addressable opportunity.