About Achondroplasia Treatment
Achondroplasia is a rare genetic bone disorder. It causes the strong, flexible tissue called cartilage to not be made into bone as normal. The FGFR3 gene provides fibroblast growth factor receptor 3 which is used in converting cartilage to bone. FGFR3 is only one gene associated with achondroplasia. But still, no specific treatment is available for achondroplasia. There are so much research and development happening to cure the achondroplasia. Furthermore, the growth hormone therapy is one of the treatment for achondroplasia for only a short duration of time. Increasing demand from parents who having achondroplasia boosting the demand for achondroplasia treatment.
Attributes | Details |
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Study Period | 2018-2030 |
Base Year | 2023 |
Unit | Value (USD Million) |
Key players are adopting numerous strategies to gain market attention and to increase their market share, this strategy can be listed as increasing product portfolio, making partnerships to adopt certain technologies, and acquiring small players to finish the competition in the future. As well as investing money in the R&D sector to make technical upgrades to the product. Analyst at AMA Research estimates that United States Players will contribute the maximum growth to Global Achondroplasia Treatment market throughout the forecasted period. Established and emerging Players should take a closer view at their existing organizations and reinvent traditional business and operating models to adapt to the future.
Ascendis Pharma A/S (Denmark), BioMarin Pharmaceutical Inc (United States), Ribomic Inc (Japan) and Ultragenyx Pharmaceutical Inc (United States) are some of the key players that are part of study coverage.
Segmentation Overview
AMA Research has segmented the market of Global Achondroplasia Treatment market by Type (RBM-007, TA-46, B-701 and Others), Application (Hospital, Clinic and Others) and Region.
On the basis of geography, the market of Achondroplasia Treatment has been segmented into South America (Brazil, Argentina, Rest of South America), Asia Pacific (China, Japan, India, South Korea, Taiwan, Australia, Rest of Asia-Pacific), Europe (Germany, France, Italy, United Kingdom, Netherlands, Rest of Europe), MEA (Middle East, Africa), North America (United States, Canada, Mexico).
Influencing Trend:
Achondroplasia Diagnosed after Birth with a Physical Exam
Market Growth Drivers:
Rising Incidences of Achondroplastic Dwarfism, Growing Concern Towards Physical Characteristics and Increasing Disposable Income in Emerging Countries
Challenges:
After Treatment Chances of Causing Unexpected New Mutations
Restraints:
Lack of Awareness related to Treatment
Opportunities:
Increasing Demand from the Parents who already Having an Achondroplasia and To Relieve Problems Caused by Achondroplasia Increasing Demand of the Surgeries such as Treat Hunchback, Lengthen the Legs, Treat Bowing of the Legs
Market Leaders and their expansionary development strategies
In July 2023, BioMarin Pharmaceutical and Pfizer announced a collaboration to develop and commercialize a gene therapy treatment for achondroplasia. This partnership combines BioMarin's expertise in rare diseases with Pfizer's gene therapy capabilities, accelerating the development of this promising therapy.
In October 2023, several leading pharmaceutical companies, patient advocacy groups, and academic institutions formed the Achondroplasia Clinical Research Collaboration Network (ACRCN). This network aims to streamline and accelerate clinical research for achondroplasia by sharing data, resources, and expertise.
Key Target Audience
Achondroplasia Treatment manufacturers, Traders, Importer, and Exporter, Raw material suppliers and distributors, Research and consulting firms, Government and research organizations and Associations and industry bodies
About Approach
To evaluate and validate the market size various sources including primary and secondary analysis is utilized. AMA Research follows regulatory standards such as NAICS/SIC/ICB/TRCB, to have a better understanding of the market. The market study is conducted on basis of more than 200 companies dealing in the market regional as well as global areas with the purpose to understand the companies positioning regarding the market value, volume, and their market share for regional as well as global.
Further to bring relevance specific to any niche market we set and apply a number of criteria like Geographic Footprints, Regional Segments of Revenue, Operational Centres, etc. The next step is to finalize a team (In-House + Data Agencies) who then starts collecting C & D level executives and profiles, Industry experts, Opinion leaders, etc., and work towards appointment generation.
The primary research is performed by taking the interviews of executives of various companies dealing in the market as well as using the survey reports, research institute, and latest research reports. Meanwhile, the analyst team keeps preparing a set of questionnaires, and after getting the appointee list; the target audience is then tapped and segregated with various mediums and channels that are feasible for making connections that including email communication, telephonic, skype, LinkedIn Group & InMail, Community Forums, Community Forums, open Survey, SurveyMonkey, etc.