About Gene Therapy
Genes are composed of DNA (Deoxyribonucleic Acid) that contains important information for making proteins which are vital for optimal human body function. Certain gene alterations result in these proteins not being made properly & so can lead to genetic disorders. Gene therapy is a new technique which uses genes to prevent or treat disease. Over the coming years, this technique may permit doctors to treat a disorder by inserting a gene into a patient’s cells rather than using drugs or surgery. This new therapy works by repairing, repressing, or replacing dysfunctional genes which cause disease with aiming of reestablishing normal function. Gene therapy is a striking area for drug development. With the right target & approach, it can address the original cause of a severe diseases.
Attributes | Details |
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Study Period | 2018-2030 |
Base Year | 2023 |
Unit | Value (USD Million) |
CAGR | 19.3% |
Major players operating in the global gene therapy market are conducting various clinical and pre-clinical developmental stages of gene therapies. For Instance, In November 2018, Novartis International AG has announced that the EC (European Commission) approved Luxturna, a one time gene therapy aimed at the treatment of patients with vision loss owing to a genetic mutation in both copies of the RPE65 gene as well as who have enough viable retinal cells. The authorization is valid in all 28 member states of the European Commission, & Iceland, Liechtenstein as well as Norway. Luxturna was developed & is commercialized in the United States by Spark Therapeutics. Analyst at AMA Research estimates that French, United Kingdom, and United States Players will contribute the maximum growth to Global Gene Therapy market throughout the forecasted period. Established and emerging Players should take a closer view at their existing organizations and reinvent traditional business and operating models to adapt to the future.
Novartis International AG (Switzerland), Kite Pharma, Inc. (United States), Spark Therapeutics Inc. (United States), GlaxoSmithKline PLC (United Kingdom), Bluebird bio Inc. (United States), Genethon (France), Transgene SA (France), Applied Genetic Technologies Corporation (United States), Oxford BioMedica (United Kingdom) and NewLink Genetics Corporation (United States) are some of the key players that are part of study coverage. Additionally, the Players which are also part of the research coverage are Sangamo Therapeutics, Inc. (United States), UniQure N.V (Netherlands) and Celgene Corporation (United States).
Segmentation Overview
AMA Research has segmented the market of Global Gene Therapy market by Type (Somatic Cell Gene Therapy and Germ Cell Gene Therapy), Application (Neurological Disorders, Rare Diseases, Oncological Disorders, Cardiovascular Diseases, Infectious disease and Other Diseases) and Region.
On the basis of application, Oncological Disorders segment is dominating the market in the year 2023On the basis of geography, the market of Gene Therapy has been segmented into South America (Brazil, Argentina, Rest of South America), Asia Pacific (China, Japan, India, South Korea, Taiwan, Australia, Rest of Asia-Pacific), Europe (Germany, France, Italy, United Kingdom, Netherlands, Rest of Europe), MEA (Middle East, Africa), North America (United States, Canada, Mexico). North America region held largest market share in the year 2023. If we see Market by Vector Type, the sub-segment i.e. Viral Vector will boost the Gene Therapy market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth.
Market Growth Drivers:
Rising Investment for R&D Activities Relating to Gene Therapy, Growing Prevalence of Cancer and Increasing Awareness Regarding Gene Therapy
Restraints:
High Cost Related With Gene Therapies and Undesirable Immune Responses
Opportunities:
Untapped Potential for Emerging Markets and Ongoing Advancements in Gene Therapy
Market Leaders and their expansionary development strategies
In January 25, 2024, WuXi AppTec and WuXi Advanced Therapies (WAT) enter into a strategic partnership with Rocket Pharmaceuticals to develop and manufacture gene therapies for rare diseases
In October 26, 2023: Thermo Fisher Scientific launches a new single-use bioreactor system designed for the efficient production of viral vectors for gene therapies.
Analyst View
On the basis of vector type, the global gene therapy market is divided into viral vector [Adenoviruses, Retroviruses, Lentiviruses, Adeno Associated Virus, Herpes Simplex Virus, Poxvirus, Vaccinia Virus, and Others], as well as non-viral vector [Gene Gun, Naked/Plasmid Vectors, Electroporation, Lipofection, and Others].
Key Target Audience
Gene Therapy providers, Government and Research Organizations, Industry Associations, Regulatory Bodies, Pharmaceutical Companies and Others
About Approach
To evaluate and validate the market size various sources including primary and secondary analysis is utilized. AMA Research follows regulatory standards such as NAICS/SIC/ICB/TRCB, to have a better understanding of the market. The market study is conducted on basis of more than 200 companies dealing in the market regional as well as global areas with the purpose to understand the companies positioning regarding the market value, volume, and their market share for regional as well as global.
Further to bring relevance specific to any niche market we set and apply a number of criteria like Geographic Footprints, Regional Segments of Revenue, Operational Centres, etc. The next step is to finalize a team (In-House + Data Agencies) who then starts collecting C & D level executives and profiles, Industry experts, Opinion leaders, etc., and work towards appointment generation.
The primary research is performed by taking the interviews of executives of various companies dealing in the market as well as using the survey reports, research institute, and latest research reports. Meanwhile, the analyst team keeps preparing a set of questionnaires, and after getting the appointee list; the target audience is then tapped and segregated with various mediums and channels that are feasible for making connections that including email communication, telephonic, skype, LinkedIn Group & InMail, Community Forums, Community Forums, open Survey, SurveyMonkey, etc.