About Ataxia-Telangiectasia
Ataxia-Telangiectasia is a unique and rare genetic disorder occurring in children. Ataxia disease denotes uncoordinated movements during walking while Telangiectasia refers to a situation when the child has enlarged blood vessels beneath the skin. The veins in the disease appear to be red and they spread like a spider in Telangiectasia. This disease is genetically inherited from an autosomal recessive trait. It develops in children when both the parents lack a copy of the non-functional gene. The affected patients are likely to have high amounts of alpha-fetoprotein present in their blood. The effect of this protein is in people is unknown. This disease is the effect of mutation of the ATM gene in the affected body. The gene is responsible for the production of a protein that regulated the growth and the division of cells in the body. Several other problems associated with the following disease are the imbalance of walking, hand coordination, jerky movements, muscle twitching, and disturbed nerve functioning which makes it difficult for the child to do several activities normally and at a faster pace. The patients often require wheel-chair support to deal with the disease at an early age.
Attributes | Details |
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Study Period | 2018-2030 |
Base Year | 2023 |
Unit | Value (USD Million) |
The companies are exploring the market by adopting mergers & acquisitions, expansions, investments, new service launches, and collaborations as their preferred strategies. The players are exploring new geographies through expansions and acquisitions to avail a competitive advantage through combined synergies. Analyst at AMA Research estimates that Asian Players will contribute the maximum growth to Global Ataxia-Telangiectasia market throughout the forecasted period. Established and emerging Players should take a closer view at their existing organizations and reinvent traditional business and operating models to adapt to the future.
Sanofi (France), Intrabio Ltd (United Kingdom), Intas Pharmaceuticals Ltd (India), Sun Pharmaceutical Industries Ltd (India), Cipla Inc (India), Eli Lilly and Company (United States), Saol Therapeutics Inc. (United States) and USV Private Limited (India) are some of the key players that are part of study coverage.
Segmentation Overview
AMA Research has segmented the market of Global Ataxia-Telangiectasia market by and Region.
On the basis of geography, the market of Ataxia-Telangiectasia has been segmented into South America (Brazil, Argentina, Rest of South America), Asia Pacific (China, Japan, India, South Korea, Taiwan, Australia, Rest of Asia-Pacific), Europe (Germany, France, Italy, United Kingdom, Netherlands, Rest of Europe), MEA (Middle East, Africa), North America (United States, Canada, Mexico). If we see Market by Distribution Channel, the sub-segment i.e. Hospital Pharmacies will boost the Ataxia-Telangiectasia market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth. If we see Market by Diagnosis Type, the sub-segment i.e. IgA and Serum Alpha-1 Fetoprotein Levels will boost the Ataxia-Telangiectasia market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth. If we see Market by Treatment Type, the sub-segment i.e. Oral Tablets will boost the Ataxia-Telangiectasia market. Additionally, the rising demand from SMEs and various industry verticals gives enough cushion to market growth.
Influencing Trend:
Increased Research and Development in Automated Health Care Solutions
Market Growth Drivers:
Increase in Investment for Research and Development for the Treatment, Increase in the Prevalence Rate and Increased Rate of Child Birth
Challenges:
Lack of Awareness About Genetic-Disorders in Under-Developed Countries
Restraints:
High Cost of Diagnosis and Lack of Skilled Health Care Professionals
Opportunities:
Potential for Development of New Treatments in Under Developed Countries
Market Leaders and their expansionary development strategies
On September 12, 2023, Roche received FDA approval for Tecentriq (atezolizumab) in combination with Avastin (bevacizumab) for the treatment of non-small cell lung cancer (NSCLC) in patients with AT mutations. While not directly targeting AT itself, this approval highlights the potential of targeting related pathways for symptom management.
In October 2023, ATAI Life Sciences announced the launch of their GeneRepair platform, a gene editing technology with potential applications in treating AT and other genetic diseases. They are currently seeking regulatory approval for clinical trials.
Key Target Audience
New Entrants/Investors, Analysts and Strategic Business Planners, Providers of Ataxia-Telangiectasia Treatment, Venture Capitalists and Private Equity Firms and End-Use Industry
About Approach
To evaluate and validate the market size various sources including primary and secondary analysis is utilized. AMA Research follows regulatory standards such as NAICS/SIC/ICB/TRCB, to have a better understanding of the market. The market study is conducted on basis of more than 200 companies dealing in the market regional as well as global areas with the purpose to understand the companies positioning regarding the market value, volume, and their market share for regional as well as global.
Further to bring relevance specific to any niche market we set and apply a number of criteria like Geographic Footprints, Regional Segments of Revenue, Operational Centres, etc. The next step is to finalize a team (In-House + Data Agencies) who then starts collecting C & D level executives and profiles, Industry experts, Opinion leaders, etc., and work towards appointment generation.
The primary research is performed by taking the interviews of executives of various companies dealing in the market as well as using the survey reports, research institute, and latest research reports. Meanwhile, the analyst team keeps preparing a set of questionnaires, and after getting the appointee list; the target audience is then tapped and segregated with various mediums and channels that are feasible for making connections that including email communication, telephonic, skype, LinkedIn Group & InMail, Community Forums, Community Forums, open Survey, SurveyMonkey, etc.