Global Cystic Fibrosis Therapeutic Market Overview:
Cystic fibrosis (CF) is generally known as an inherited disease that hereby causes severe damage to the lungs, digestive system, as well as some other organs in the body. Cystic fibrosis thereby affects the cells that produce mucus, sweat, as well as digestive juices. These secreted liquids are usually thin and slippery. In people with CF, a defective gene causes secretions to become sticky and thick. Instead of acting as a lubricant, the secretions clog tubes, ducts, and passageways, especially in the lungs and pancreas. The signs and symptoms of cystic fibrosis vary depending on the severity of the condition. Even in the same person, symptoms may get worse or get better over time. Some people may not experience symptoms until they are in their teens or adulthood. An early diagnosis means that treatment can start immediately. There is as such no cure present for cystic fibrosis, but the various treatments can relieve symptoms, reduce complications, and also improve quality of life. Close monitoring and early, aggressive intervention are recommended to slow the progression of CF, which can lead to a longer lifespan. There are a number of CF therapies that can be prescribed to patients for both the lungs and the digestive tract.
Attributes | Details |
---|
Study Period | 2018-2028 |
Base Year | 2022 |
Forecast Period | 2023-2028 |
Historical Period | 2018-2022 |
Unit | Value (USD Million) |
Customization Scope | Avail customization with purchase of this report. Add or modify country, region & or narrow down segments in the final scope subject to feasibility |
Influencing Trend:
Improved Healthcare Infrastructure, Reimbursements, And Initiatives and An Upsurge in The Number of Clinical Trials to Expand Its Target Patient Base with The Existing Drug Portfolio
Market Growth Drivers:
A Rise in Prevalence of Cystic Fibrosis, The Surge in Awareness About Cystic Fibrosis Across the Globe, High Public and Private Healthcare Spending, Availability of Personalized Drug Therapy & Molecular Prosthetics for The Treatment and Increasing Awareness and Better Healthcare Facilities
Challenges:
Introduction of Generic Drugs
Restraints:
High Cost of The Cystic Fibrosis Treatment and Increase in Complexity of Disease
Opportunities:
The Rising Favorable Initiatives Taken by Regional and National Nonprofit Organizations, Growing Focus on Developing Oral Routes of Administration and Increase In R&D Investments Made by Government in The Healthcare Sector
Competitive Landscape:
The companies are exploring the market by adopting mergers & acquisitions, expansions, investments, new service launches, and collaborations as their preferred strategies. The players are exploring new geographies through expansions and acquisitions to avail a competitive advantage through combined synergies.
Some of the key players profiled in the report are Genentech, Inc. (United States), Novartis AG (Switzerland), Gilead Sciences, Inc. (United States), Vertex Pharmaceuticals Incorporated (United States), AbbVie Inc. (United States), GlaxoSmithKline Plc. (United Kingdom), Johnson & Johnson (United States), Allergan plc (Ireland), Pharmaxis Ltd. (Australia) and Mylan N.V. (United States). Analyst at AMA Research see United States Players to retain maximum share of Global Cystic Fibrosis Therapeutic market by 2028. Considering Market by Route of Administration, the sub-segment i.e. Oral will boost the Cystic Fibrosis Therapeutic market. Considering Market by Drug Class, the sub-segment i.e. Pancreatic Enzyme Supplements will boost the Cystic Fibrosis Therapeutic market. Considering Market by Symptoms, the sub-segment i.e. Sputum will boost the Cystic Fibrosis Therapeutic market.
Latest Market Insights:
On February 27, 2023, AbbVie Inc. and Arrowhead Pharmaceuticals, Inc. formed a strategic alliance to develop and commercialize next-generation CF therapies using Arrowhead's RNA interference (RNAi) platform. This collaboration aims to combine AbbVie's clinical expertise in CF with Arrowhead's innovative RNAi technology to bring new treatment options to CF patients.
On March 11, 2023, Vertex Pharmaceuticals Inc. and Codexis, Inc. announced a collaboration agreement to develop novel CF therapies using Codexis's proprietary enzyme engineering technology. This partnership aims to leverage Codexis's expertise in enzyme engineering to create more effective and targeted CF treatments.
The US Food and Drug Administration had approved Trikafta (elexacaftor / ivacaftor / tezacaftor), which is the first triple combination therapy that is available for the treatment of patients with cystic fibrosis mutation. Trikafta is approved for use in patients 12 years of age and older with cystic fibrosis who have at least one F508del mutation in the Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) gene, which is an estimated 90% of the cystic fibrosis population. Trikafta also received the Orphan Drug Designation, which provides incentives to support and promote drug development for rare diseases. Drugs approved under accelerated programs are subject to the same approval standards as other FDA approvals.
What Can be Explored with the Cystic Fibrosis Therapeutic Market Study
Gain Market Understanding
Identify Growth Opportunities
Analyze and Measure the Global Cystic Fibrosis Therapeutic Market by Identifying Investment across various Industry Verticals
Understand the Trends that will drive Future Changes in Cystic Fibrosis Therapeutic
Understand the Competitive Scenario
- Track Right Markets
- Identify the Right Verticals
Research Methodology:
The top-down and bottom-up approaches are used to estimate and validate the size of the Global Cystic Fibrosis Therapeutic market.
In order to reach an exhaustive list of functional and relevant players various industry classification standards are closely followed such as NAICS, ICB, SIC to penetrate deep in important geographies by players and a thorough validation test is conducted to reach most relevant players for survey in Cystic Fibrosis Therapeutic market.
In order to make priority list sorting is done based on revenue generated based on latest reporting with the help of paid databases such as Factiva, Bloomberg etc.
Finally the questionnaire is set and specifically designed to address all the necessities for primary data collection after getting prior appointment by targeting key target audience that includes New Entrants/Investors, Analysts and Strategic Business Planners, Providers of Cystic Fibrosis Therapeutic, Venture Capitalists and Private Equity Firms, Government Regulatory and Research Organizations and End-Use Industry.
This helps us to gather the data related to players revenue, operating cycle and expense, profit along with product or service growth etc.
Almost 70-80% of data is collected through primary medium and further validation is done through various secondary sources that includes Regulators, World Bank, Association, Company Website, SEC filings, OTC BB, USPTO, EPO, Annual reports, press releases etc.