Market Snapshot:
A rare disease is a group of conditions that affect very small numbers of people. Rare diseases affect approximately 6-10% of the population and 3-4% of births. It tends to be severe, chronic conditions and in many cases, they are progressive, debilitating, and life-threatening. Patient access to the treatment, including medicines, is access to healthcare professionals and a healthcare infrastructure that fosters the correct diagnosis. On average, a treatment for a rare disease costs USD137,000 per person per year. According to the WHO, rare diseases range from cystic fibrosis and haemophilia to angelman syndrome, with an incidence of about 1 in 15 000, to Opitz trigonocephaly syndrome. It is extremely rare with about one case per million people. Most people suffering from rare diseases do not have any treatment options available for their condition. (It is estimated that 95% of rare diseases do not have a treatment option.) In March 2020, FDA grants experimental coronavirus drug benefits for rare disease treatments.
Highlights from Rare Disease Treatment Market Study
Attributes | Details |
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Study Period | 2018-2030 |
Base Year | 2023 |
Unit | Value (USD Million) |
The key Players profiled in the report are Bristo Myers Squibb (Celgene Corporation), F. Hoffmann-La Roche Ltd., Novartis AG, Merck, AbbVie, Johnson & Johnson (Janssen global services, LLC), Vertex Pharmaceutical, Sanofi, Pfizer, Inc., AstraZeneca, Eli Lilly, Tekeda, Amgen Inc., Gilead Sciences, Inc and Others.
Geographic Breakdown and Segment Analysis
The Global Rare Disease Treatment market presents a comprehensive analysis of the Rare Disease Treatment market by product type (Cancer, -Non-Hodgkin Lymphoma, -Acute Myeloid Leukemia, -Pancreatic Cancer, -Ovarian Cancer, -Multiple Myeloma, -Renal Cell Carcinoma, -Others, Metabolic Diseases, Hematologic & Immunologic Diseases, Infectious Diseases, Neurologic Diseases and Others), by end-user/application (Hospitals, Clinics and Others), and by geography (North America, South America, Europe, Asia-Pacific and MEA) along with country level break-up. This section of our report presents a realistic picture of the Global Rare Disease Treatment industry. Investors and Players can easily understand the inherent opportunities and challenges for their products in geographical region of interest.
For instance, while the holds majority of market share of the Rare Disease Treatment market
Analyst at AMA have segmented the market study of Global Rare Disease Treatment market by Type, Application and Region.
Influencing Trend:
Growing Research Activities and the Increasing focus on the Development of New Therapeutics and Drugs, Sustainable Access to Diagnosis, Treatment and and Care
Market Growth Drivers:
Increasing Geriatric Population and the Rising Focus of the Players on the Enhancement of the Medical Facilities and Rising Awareness among People about Efficient Treatment Methods to Treat Rare Diseases
Challenges:
Rare diseases pose challenges for research and clinical development due to the small numbers of patients, limited epidemiological data on the natural history of many rare diseases, and all stages of research and development being more challenging and lengthy than for more, common diseases. and Lack of Skilled Healthcare Personnel
Restraints:
Delays and Frequent Errors in Diagnosis, often with Severe Consequences for Patient Outcomes
Opportunities:
Greater Collaboration at all Levels Will Help Drive Research, and Improve Care and Rising Investment of Research and Development on the Rare Disease Treatments
Market Developments Activities:
In Feb 2019, Ipsen announced the acquisition of the Clementia Pharmaceuticals for the treatment of the key late-stage clinical asset palovarotene, multiple osteochondromas, and others. Through this agreement, the company is aiming to enhance its product portfolio in rare diseases across the globe.
Key Target Audience
Venture Capitalists and Private Equity Firms, New Entrants/Investors, Analysts and Strategic Business Planners, Rare Disease Drug Manufacturers, Suppliers and Distributors, Raw Material Suppliers, Government Regulatory and Research Organizations and End-Use Industries